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Added to YB: 2026-02-10

Pitch date: 2026-02-06

RGNX [neutral]

REGENXBIO Inc.

-17.06%

current return

Author Info

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Company Info

REGENXBIO Inc., a clinical-stage biotechnology company, provides gene therapies that deliver functional genes to cells with genetic defects in the United States.

Market Cap

$522.9M

Pitch Price

$10.14

Price Target

N/A

Dividend

N/A

EV/EBITDA

-3.90

P/E

-2.98

EV/Sales

3.03

Sector

Biotechnology

Category

special_situation

Show full summary:
Biotech Catalysts on My Radar | February 2026 - REGENXBIO Inc.

RGNX (quick overview): Gene therapy for Hunter syndrome w/ Feb 8 PDUFA date uncertain after FDA clinical hold due to CNS tumor in related RGX-111 study. RGX-121 shows strong efficacy in 30+ patients, no similar events reported. Hold based on shared vector platform. Positive outcome clears path to approval in high unmet need indication.

Read full article (2 min)